Sebastien Beauzile, 21, has been cured of sickle cell anemia, according to his doctors at Cohen’s Children’s Medical Center. Beauzile received a new gene therapy called Lyfgeni, created by the biotech ...

A Black female doctor when that was rare, she developed a diagnostic test for the disease that is still a standard tool, as well as treatment guidelines.

Two FDA-approved gene therapies, Lyfgenia and Casgevy, will be offered through an outcomes-based Medicaid model launching in January 2025. The initiative ties payments to treatment effectiveness, ...

Vertex Pharmaceuticals and bluebird bio have entered into an agreement with CMS to participate in a new Medicaid payment model for gene-based sickle cell anemia treatments, the agency announced ...

Stable production of anti-sickling adult hemoglobin (HBA T87Q) and elimination or significant reduction of vaso-occlusive events sustained through last follow-up for all evaluable patients (n=38), ...

SOMERVILLE, Mass.--(BUSINESS WIRE)--bluebird bio, Inc. (Nasdaq: BLUE) today announced that new and updated data from its lentiviral vector (LVV) gene addition programs in patients with sickle cell ...

A new type of bone marrow transplant can cure sickle cell disease with only half of the donor's cell proteins matching, according to new clinical trial results published in the New England Journal of ...

Add Yahoo as a preferred source to see more of our stories on Google. 21-year old Sebastien Beauzile becomes the first person in New York to be cured of sickle cell anemia (Screenshot: Northwell ...

When Amy Cohen, 29, finished the New York City Marathon, she broke ground as the first person with the illness to run the 26.2 mile race Mass General Brigham Amy Cohen became the first-ever person ...

Sickle cell anemia may qualify as a disability for people experiencing severe symptoms, allowing access to benefits. However, eligibility depends on how the condition affects daily life. Sickle cell ...

Sickle cell anemia is the world's most common genetic disorder. It causes the red blood pigment hemoglobin to crystallize, which results in rigid, malformed red blood cells with a sickle shape. This ...